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Development of a Gene Therapy Program for Barth Syndrome

Drs. W. Todd Cade, Christina Pacak, and colleagues have/are presenting posters at two recent scientific symposia: The Keystone Symposia on Molecular and Cellular Biology, Rare and Undiagnosed Diseases: Discovery and Models of Precision Therapy; and The American Society of Gene & Cell Therapy. This poster demonstrates the advances made in getting ready for gene therapy for the treatment of Barth syndrome individuals. Learn more...

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