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Gene Therapy In Barth Syndrome: A Community Roundtable
Gene therapy holds immense promise for our community, and we invite you to join us for a conversation with Drs. Barry Byrne, Christy Pacak, and Todd Cade, to discuss the challenges facing the entire gene therapy field, from immune management to regulatory issues and trial design. We also welcome your questions to pose to our presenters for the webinar.
