Join Barth Syndrome Foundation (BSF) in its cornerstone, multi-track event that brings researchers, clinicians, and families from around the world together in solidarity to further our global mission. Learn more
On November 8, 2021, Dr. Colin Steward (Emeritus, U. Bristol), Dr. Guido Pieles (U. Bristol), Dr. Barney Reeves and Lucy Dabner (Bristol Trials Centre) discussed the research basis, findings, challenges, and successes for the UK-based CARDIOMAN trial. Sponsored by the UK National Institute for Health Research, co-funded by BSF, informed, designed, and led by long-time academic research leaders in our field, and ultimately made possible by the initial participation of eleven affected individuals - this nearly 8-year effort encapsulates the adage that it takes a village.
BSF's Executive Director, Emily Milligan, wrote to Stealth BioTherapeuitic's leadership after the FDA refused to file the NDA for elamipretide. To read the full letter, click the title above.
Barth Syndrome Foundation is a global facilitator for advancing understanding of and developing treatments for Barth syndrome.
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